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Giuseppe Ronzitti

5
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  • 1042365
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"fboisgerault"
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Long-term correction of ornithine transcarbamylase deficiency in Spf-Ash mice with a translationally optimized AAV vector

Marcelo Simon Sola , Takashi Kei Kishimoto , Giulia de Sabbata , Florence Boisgérault , Corrado Guarnaccia
Molecular Therapy - Methods and Clinical Development, 2021, 20, pp.169 - 180. ⟨10.1016/j.omtm.2020.11.005⟩
Article dans une revue hal-03193757v1
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Antigen-selective modulation of AAV immunogenicity with tolerogenic rapamycin nanoparticles enables successful vector re-administration

Florence Boisgérault , Amine Meliani , Romain Hardet , Solenne Marmier , Fanny Collaud
Nature Communications, 2018, 9 (1), pp.4098. ⟨10.1038/s41467-018-06621-3⟩
Article dans une revue hal-02177709v1
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Autophagy determines efficiency of liver-directed gene therapy with adeno-associated viral vectors

M. Hosel , A. Huber , S. Bohlen , J. Lucifora , G. Ronzitti
Hepatology, 2017, 66 (1), pp.252-265. ⟨10.1002/hep.29176⟩
Article dans une revue hal-02880988v1
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Rescue of Pompe disease in mice by AAV-mediated liver delivery of secretable acid alpha-glucosidase

F. Puzzo , P. Colella , M. G. Biferi , D. Bali , N. K. Paulk
Science Translational Medicine, 2017, 9 (418), pp.aam6375. ⟨10.1126/scitranslmed.aam6375⟩
Article dans une revue hal-02881011v1

Enhanced liver gene transfer and evasion of preexisting humoral immunity with exosome-enveloped AAV vectors

Amine Meliani , Florence Boisgérault , Zachary Fitzpatrick , Solenne Marmier , Christian Leborgne
Blood Advances, 2017, 1 (23), pp.2019-2031. ⟨10.1182/bloodadvances.2017010181⟩
Article dans une revue hal-02377508v1