guillaume corre

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Publications

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FAP-CAR-T cells reduce dystrophic muscle fibrosis, improving adeno-associated virus gene transfer efficacy

Maxime Ferrand , Céline Rocca , Guillaume Corre , Valentina Buffa , Sophie Frin et al.

Molecular Therapy - Methods and Clinical Development, 2025, 33 (3), pp.101545. ⟨10.1016/j.omtm.2025.101545⟩

Article dans une revue hal-05386318v1

Base editing of β 0 -thalassemia mutations as a therapeutic strategy for severe β-hemoglobinopathies

Giulia Hardouin , Pierre Martinucci , Samantha Scaramuzza , Panagiotis Antoniou , Federico Corradi et al.

Science Translational Medicine, 2025, 17 (826), ⟨10.1126/scitranslmed.adt8617⟩

Article dans une revue hal-05447602v1

Multiplex base editing of BCL11A regulatory elements to treat sickle cell disease

Letizia Fontana , Pierre Martinucci , Simone Amistadi , Tristan Felix , Margaux Mombled et al.

Cell Reports Medicine, 2025, 6 (10), pp.102376. ⟨10.1016/j.xcrm.2025.102376⟩

Article dans une revue hal-05447603v1

Rescue of lysosomal acid lipase deficiency in mice by rAAV8 liver gene transfer

Marine Laurent , Rim Harb , Christine Jenny , Julie Oustelandt , Simon Jimenez et al.

Communications Medicine, 2025, 5 (1), pp.110. ⟨10.1038/s43856-025-00816-8⟩

Article dans une revue hal-05447606v1
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A prime editing strategy to rewrite the γ-globin promoters and reactivate fetal hemoglobin for sickle cell disease

Anne Chalumeau , Maria Bou Dames , Letizia Fontana , Simone Amistadi , Panagiotis Antoniou et al.

Blood, 2025, 146 (22), pp.2641-2655. ⟨10.1182/blood.2024028166⟩

Article dans une revue hal-05393654v1
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Correction of exon 2, exon 2–9 and exons 8–9 duplications in DMD patient myogenic cells by a single CRISPR/Cas9 system

Juliette Lemoine , Auriane Dubois , Alan Dorval , Abbass Jaber , Ganesh Warthi et al.

Scientific Reports, 2024, 14 (1), pp.21238. ⟨10.1038/s41598-024-70075-5⟩

Article dans une revue hal-04795480v1

An empowered, clinically viable hematopoietic stem cell gene therapy for the treatment of multisystemic mucopolysaccharidosis type II

Sabyasachi Das , Fatlum Rruga , Annita Montepeloso , Agnese Dimartino , Silvia Spadini et al.

Molecular Therapy, 2024, 32 (3), pp.619-636. ⟨10.1016/j.ymthe.2024.01.034⟩

Article dans une revue hal-04954229v1
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Evaluation of diversity indices to estimate clonal dominance in gene therapy studies

Guillaume Corre , Anne Galy

Molecular Therapy - Methods and Clinical Development, 2023, 29, pp.418-425. ⟨10.1016/j.omtm.2023.05.003⟩

Article dans une revue hal-04324363v1
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Global genome decompaction leads to stochastic activation of gene expression as a first step toward fate commitment in human hematopoietic cells

Romuald Parmentier , Laëtitia Racine , Alice Moussy , Sophie Chantalat , Ravi Sudharshan et al.

PLoS Biology, 2022, 20 (10), pp.e3001849. ⟨10.1371/journal.pbio.3001849⟩

Article dans une revue hal-04025552v1
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Deciphering the Molecular Mechanism of Incurable Muscle Disease by a Novel Method for the Interpretation of miRNA Dysregulation

David Israeli , Ai Vu Hong , Guillaume Corre , Quentin Miagoux , Isabelle Richard

Non-Coding RNA, 2022, 8 (4), pp.48. ⟨10.3390/ncrna8040048⟩

Article dans une revue hal-03874746v1

Lentiviral standards to determine the sensitivity of assays that quantify lentiviral vector copy numbers and genomic insertion sites in cells

Guillaume Corre , Ababacar Seye , Sophie Frin , Maxime Ferrand , Kathrin Winkler et al.

Gene Therapy, 2022, 29 (9), pp.536-543. ⟨10.1038/s41434-022-00315-8⟩

Article dans une revue hal-04955303v1
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Cholesterol metabolism is a potential therapeutic target in Duchenne muscular dystrophy

Fatima Amor , Ai Vu Hong , Guillaume Corre , Mathilde Sanson , Laurence Suel et al.

Journal of Cachexia, Sarcopenia and Muscle, 2021, 12 (3), pp.677-693. ⟨10.1002/jcsm.12708⟩

Article dans une revue hal-03335763v1
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Ex vivo editing of human hematopoietic stem cells for erythroid expression of therapeutic proteins

Giulia Pavani , Marine Laurent , Anna Fabiano , Erika Cantelli , Aboud Sakkal et al.

Nature Communications, 2020, 11 (1), pp.3778. ⟨10.1038/s41467-020-17552-3⟩

Article dans une revue inserm-02946890v1
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miR-379 links glucocorticoid treatment with mitochondrial response in Duchenne muscular dystrophy

Mathilde Sanson , Ai Vu Hong , Emmanuelle Massourides , Nathalie Bourg , Laurence Suel et al.

Scientific Reports, 2020, 10 (1), pp.9139. ⟨10.1038/s41598-020-66016-7⟩

Article dans une revue inserm-02881214v1

Titin splicing regulates cardiotoxicity associated with calpain 3 gene therapy for limb-girdle muscular dystrophy type 2A

William Lostal , Carinne Roudaut , Marine Faivre , Karine Charton , Laurence Suel et al.

Science Translational Medicine, 2019, 11 (520), pp.eaat6072. ⟨10.1126/scitranslmed.aat6072⟩

Article dans une revue hal-03335723v1
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An AAV-SGCG Dose-Response Study in a γ-Sarcoglycanopathy Mouse Model in the Context of Mechanical Stress

David Israeli , Jérémie Cosette , Guillaume Corre , Fatima Amor , Jérôme Poupiot et al.

Molecular Therapy - Methods and Clinical Development, 2019, 13, pp.494-502. ⟨10.1016/j.omtm.2019.04.007⟩

Article dans une revue hal-02178338v1
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Temporary Reduction of Membrane CD4 with the Antioxidant MnTBAP Is Sufficient to Prevent Immune Responses Induced by Gene Transfer

S. da Rocha , J. Bigot , F. Onodi , Jérémie Cosette , Guillaume Corre et al.

Molecular Therapy - Methods and Clinical Development, 2019, 14, pp.285-299. ⟨10.1016/j.omtm.2019.06.011⟩

Article dans une revue hal-02880792v1

Constraints on Human CD34+ Cell Fate due to Lentiviral Vectors Can Be Relieved by Valproic Acid

Alice Moussy , Nan Papili Gao , Guillaume Corre , Valentina Poletti , Saliha Majdoul et al.

Human Gene Therapy, 2019, ⟨10.1089/hum.2019.009⟩

Article dans une revue hal-02178315v1

Species-specific titin splicing regulates cardiotoxicity associated with calpain 3 gene therapy for limb-girdle muscular dystrophy 2A

William Lostal , Carinne Roudaut , Marine Faivre , Karine Charton , Laurence Suel et al.

Science Translational Medicine, 2019, 11 (520), pp.eaat6072. ⟨10.1126/scitranslmed.aat6072⟩

Article dans une revue hal-02408897v1
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Genome Editing of Expanded CTG Repeats within the Human DMPK Gene Reduces Nuclear RNA Foci in the Muscle of DM1 Mice

Mirella Lo Scrudato , Karine Poulard , Célia Sourd , Stéphanie Tomé , Arnaud Klein et al.

Molecular Therapy, 2019, Epub ahead of print. ⟨10.1016/j.ymthe.2019.05.021⟩

Article dans une revue hal-02177548v1
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Preclinical Development of a Lentiviral Vector for Gene Therapy of X-Linked Severe Combined Immunodeficiency

Valentina Poletti , Sabine Charrier , Guillaume Corre , Bernard Gjata , Alban Vignaud et al.

Molecular Therapy - Methods and Clinical Development, 2018, 9, pp.257-269. ⟨10.1016/j.omtm.2018.03.002⟩

Article dans une revue hal-02178311v1
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Pre-clinical Development of a Lentiviral Vector Expressing the Anti-sickling βAS3 Globin for Gene Therapy for Sickle Cell Disease

Valentina Poletti , Fabrizia Urbinati , Sabine Charrier , Guillaume Corre , Roger Hollis et al.

Molecular Therapy - Methods and Clinical Development, 2018, 11, pp.167-179. ⟨10.1016/j.omtm.2018.10.014⟩

Article dans une revue hal-02178306v1
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Integrated time-lapse and single-cell transcription studies highlight the variable and dynamic nature of human hematopoietic cell fate commitment

Alice Moussy , Jérémie Cosette , Romuald Parmentier , Cindy da Silva , Guillaume Corre et al.

PLoS Biology, 2017, 15 (7), ⟨10.1371/journal.pbio.2001867⟩

Article dans une revue hal-01934491v1
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Long-term exposure to Myozyme results in a decrease of anti-drug antibodies in late-onset Pompe disease patients

Elisa Masat , Pascal Laforêt , Marie de Antonio , Guillaume Corre , Barbara Perniconi et al.

Scientific Reports, 2016, 6, pp.36182. ⟨10.1038/srep36182⟩

Article dans une revue hal-01404918v1
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Systemic epigenetic response to recombinant lentiviral vectors independent of proviral integration

Tamas Aranyi , Daniel Stockholm , Roseline Yao , Catherine Poinsignon , Thibaut Wiart et al.

Epigenetics & Chromatin, 2016, 9 (1), ⟨10.1186/s13072-016-0077-1⟩

Article dans une revue hal-02178319v1

“RCL-Pooling Assay”: A Simplified Method for the Detection of Replication-Competent Lentiviruses in Vector Batches Using Sequential Pooling

Guillaume Corre , Michel Dessainte , Jean-Brice Marteau , Bruno Dalle , David Fenard et al.

Human Gene Therapy, 2016, 27 (2), pp.202-210. ⟨10.1089/hum.2015.166⟩

Article dans une revue hal-02178335v1

Efficacité et sécurité du traitement par thérapie génique des patients atteints du syndrome de Wiskott-Aldrich

Anne Galy , Guillaume Corre , Marina Cavazzana , Salima Hacein-Bey-Abina

Médecine/Sciences, 2015, 31 (12), pp.1066-1069. ⟨10.1051/medsci/20153112006⟩

Article dans une revue hal-02178298v1

Hypoxic culture conditions enhance the generation of regulatory T cells

Thi My Anh Neildez-Nguyen , Jérémy Bigot , Sylvie da Rocha , Guillaume Corre , Florence Boisgérault et al.

Immunology, 2015, 144 (3), pp.431-443. ⟨10.1111/imm.12388⟩

Article dans une revue hal-02178266v1
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Serotype-specific Binding Properties and Nanoparticle Characteristics Contribute to the Immunogenicity of rAAV1 Vectors

Maxime Ferrand , Sylvie da Rocha , Guillaume Corre , Anne Galy , Florence Boisgérault

Molecular Therapy, 2015, 23 (6), pp.1022-1033. ⟨10.1038/mt.2015.59⟩

Article dans une revue hal-02178340v1
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Stochastic Fluctuations and Distributed Control of Gene Expression Impact Cellular Memory

Guillaume Corre , Daniel Stockholm , Ophélie Arnaud , Gaël Kaneko , José Viñuelas et al.

PLoS ONE, 2014, 9 (12), pp.e115574. ⟨10.1371/journal.pone.0115574⟩

Article dans une revue hal-01370311v1

Lentiviral Transduction of CD34+ Cells Induces Genome-Wide Epigenetic Modifications

Yoshiaki Yamagata , Véronique Parietti , Daniel Stockholm , Guillaume Corre , Catherine Poinsignon et al.

PLoS ONE, 2012, 7 (11), pp.e48943. ⟨10.1371/journal.pone.0048943⟩

Article dans une revue hal-02177572v1

Bistable Cell Fate Specification as a Result of Stochastic Fluctuations and Collective Spatial Cell Behaviour

Daniel Stockholm , Frédérique Edom-Vovard , Sophie Coutant , Peggy Sanatine , Yoshiaki Yamagata et al.

PLoS ONE, 2010, 5 (12), pp.e14441. ⟨10.1371/journal.pone.0014441⟩

Article dans une revue hal-02178248v1