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Drug Candidate BIO101 for Spinal Muscular Atrophy as Monotherapy or Combined With the Antisense Oligonucleotide ASO‐10‐27
Cynthia Bézier
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Steve Cottin
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Parvin Nazari Hashemi
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Mirella El Khoury
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Zoé Clerc
et al.
Article dans une revue
hal-05453886
v1
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Combining SMN2 splicing modifiers with HDAC6 inhibition greatly improves muscle function and survival in Spinal Muscular Atrophy
Alexis Osseni
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Rasha Slika
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Laurent Coudert
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Agnes Conjard-Duplany
,
Laure Weill
et al.
Article dans une revue
hal-05044738
v1
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The analysis of the skeletal muscle metabolism is crucial for designing optimal exercise paradigms in type 2 diabetes mellitus
Elias Abi Akar
,
Laure Weill
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Mirella El Khoury
,
Cédric Caradeuc
,
Gildas Bertho
et al.
Article dans une revue
hal-05316643
v1
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Dysregulation of muscle cholesterol transport in amyotrophic lateral sclerosis
D. Sapaly
,
F. Cheguillaume
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L. Weill
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Z. Clerc
,
O. Biondi
et al.
Article dans une revue
hal-04977711
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NADPH oxidase 4 inhibition is a complementary therapeutic strategy for spinal muscular atrophy
Mirella El Khoury
,
Olivier Biondi
,
Gaelle Bruneteau
,
Delphine Sapaly
,
Sabrina Bendris
et al.
Article dans une revue
hal-04495927
v1
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Activating ATF6 in spinal muscular atrophy promotes SMN expression and motor neuron survival through the IRE1α‐XBP1 pathway
Domenico d'Amico
,
Olivier Biondi
,
Camille Januel
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Cynthia Bezier
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Delphine Sapaly
et al.
Article dans une revue
inserm-04385529
v1
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The Small-Molecule Flunarizine in Spinal Muscular Atrophy Patient Fibroblasts Impacts on the Gemin Components of the SMN Complex and TDP43, an RNA-Binding Protein Relevant to Motor Neuron Diseases
Delphine Sapaly
,
Perrine Delers
,
Jennifer Coridon
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Badih Salman
,
Franck Letourneur
et al.
Article dans une revue
hal-05453823
v1
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Low-Intensity Running and High-Intensity Swimming Exercises Differentially Improve Energy Metabolism in Mice With Mild Spinal Muscular Atrophy
Léo Houdebine
,
Domenico d'Amico
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Jean Bastin
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Farah Chali
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Céline Desseille
et al.
Article dans une revue
inserm-02893893
v1
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Small-molecule flunarizine increases SMN protein in nuclear Cajal bodies and motor function in a mouse model of spinal muscular atrophy
Delphine Sapaly
,
Matthieu Dos Santos
,
Perrine Delers
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Olivier Biondi
,
Gwendoline Quérol
et al.
Article dans une revue
pasteur-02090360
v1
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